Therapeutic approach that involves inserting nucleic acids into the patient's cells.
1Jake was one of 13 patients given pioneering gene therapy last year.
2Episomally maintained self-replicating systems present attractive alternative vehicles for gene therapy applications.
3Background: Vascular gene therapy requires safe and efficient gene transfer in vivo.
4This method will contribute to future gene therapy for age-related macular degeneration.
5This virus also offers a potential liver-specific targeting system for gene therapy.
6Both safety and efficacy have held back the field of gene therapy.
7Genetic diagnosis is essential for pathogenic understanding and for gene therapy development.
8Background: The outcomes of gene therapy to correct congenital immunodeficiencies are unknown.
9No significant toxic effects due to the IL-12 gene therapy were observed.
10Among the goals of gene therapy is long-term expression of delivered transgenes.
11These studies may have implications for pFVIII gene therapy in hemophilia A.
12About Krystal Biotech Inc Krystal Biotech, Inc. is a gene therapy company.
13The rAAV-kallistatin gene therapy significantly inhibited tumor cell proliferation and induced apoptosis.
14UniQure is not the first gene therapy firm to float on Nasdaq.
15This property makes minicircle DNA an excellent vector for non-viral gene therapy.
16Next, we assessed the efficacy of in situ gene therapy with Ad.
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Translations for gene therapy